A LAYTOWN family is racing against time to raise €2.7 million for life-changing treatment in the United States for their ...

Some children in Northern Ireland who live with a severe form of muscular dystrophy will be able to access new medication on the health service, BBC News understands. The move from the Belfast Health ...

BRAINERD — Motorcycle riders and enthusiasts from across the world will soon descend on Brainerd as they work to raise awareness and fight Duchenne muscular dystrophy. Hosted by Brainerd's Craig ...

Please provide your email address to receive an email when new articles are posted on . At the time of last follow up, 82.6% of children born with SMA type 1 from 2016 on were still alive. Of the 140 ...

LONG ISLAND (WABC) -- On Monday there are growing calls for leniency as many say the Department of Government Efficiency is going too far. Doctors and researchers say the trimming is about much more ...

What Is Itvisma, and Why Does It Matter? Itvisma (onasemnogene abeparvovec-brve) is a gene therapy that the FDA has approved to treat spinal muscular atrophy (SMA) in adults, teens, and children 2 or ...

"Our preliminary findings show that German children with SMA, despite significant physical disability, have surprisingly good subjective HRQoL." – Erik Landfeldt, MSc, PhD Previous studies have found ...

Gene therapies have extended survival in muscular dystrophy, requiring improved care transitions from pediatric to adult systems. Current systems lack adequate staffing, specialists, and communication ...

LOUISVILLE, Ky. (WDRB) — The Louisville Fire Department is raising money for kids living with muscular dystrophy. The annual "Fill the Boot" campaign was started more than 70 years ago through a ...